![Life-changing drug for babies with devastating genetic condition rejected by NICE | Muscular Dystrophy UK Life-changing drug for babies with devastating genetic condition rejected by NICE | Muscular Dystrophy UK](https://www.musculardystrophyuk.org/static/s3fs-public/styles/large_hero_image_968x545/public/Spinraza.png?VersionId=O1xBqjWUdz2mS7Kha4Sbkr8FY8xios6G&itok=WEirFWDB)
Life-changing drug for babies with devastating genetic condition rejected by NICE | Muscular Dystrophy UK
Farmalisa - Spinraza is a medicine used to treat 5q spinal muscular atrophy (SMA), a genetic disease that causes weakness and wasting of the muscles including the lung muscles. The disease is
Pharmac agrees to fund drug for those with spinal muscular atrophy after years of lobbying | RNZ News
![Zaozhuang, China. 01st Jan, 2022. (220101) -- ZAOZHUANG, Jan. 1, 2022 (Xinhua) -- Medical workers prepare to inject Spinraza to a 4-year-old child diagnosed with spinal muscular atrophy (SMA) at a hospital Zaozhuang, China. 01st Jan, 2022. (220101) -- ZAOZHUANG, Jan. 1, 2022 (Xinhua) -- Medical workers prepare to inject Spinraza to a 4-year-old child diagnosed with spinal muscular atrophy (SMA) at a hospital](https://c8.alamy.com/comp/2HCTTD3/zaozhuang-china-01st-jan-2022-220101-zaozhuang-jan-1-2022-xinhua-medical-workers-prepare-to-inject-spinraza-to-a-4-year-old-child-diagnosed-with-spinal-muscular-atrophy-sma-at-a-hospital-in-zaozhuang-east-chinas-shandong-province-jan-1-2022-china-is-striving-to-improve-the-diagnosis-and-treatment-of-rare-diseases-recently-a-tear-jerking-video-showing-how-a-national-health-insurance-negotiator-helped-cut-down-the-bidding-price-of-spinraza-from-over-53680-yuan-8422-us-dollars-per-dose-to-33000-yuan-went-viral-online-and-was-lauded-by-netizens-spinraza-a-medici-2HCTTD3.jpg)